gene therapy
Foundation Opens Door to ‘Whole Different World’ for Children with Ultra Rare Diseases
2020-12-23 17:05:15
by
Dan McCue
WASHINGTON - It began as a story no new parent wants to tell. "I always say that the day my daughter was born was the happiest day of my life, because that was the only day I didn't worry about... Read More
FDA Blocks Much-Anticipated BioMarin Hemophilia Gene Therapy
2020-08-20 14:42:36
by
FDA Blocks Much-Anticipated BioMarin Hemophilia Gene Therapy
FAIRLESS HILLS, PA (AP) — Investors fled drug developer BioMarin in droves on Wednesday, driving shares down by a third after U.S. regulators rejected the company’s potentially game-changing hemophilia A gene therapy over concerns it might not really be a... Read More
Straight From The Well
